Ahu Demir's questions to Cyclacel Pharmaceuticals (CYCC) leadership • Q2 2024
Question
Ahu Demir of Ladenburg Thalmann inquired about the clinical trial design for the fadra program, specifically asking about the enrollment targets for the CDKN2A/N2B cohort, the benchmarks for success, the expected number of patients in the upcoming data release, and whether certain genetic alterations might show more potency.
Answer
Executive Brian Schwartz explained the trial's two-stage process, stating that success in the first stage requires at least two RECIST responses in an initial cohort of 12 to 14 patients. He confirmed the company is on track to present response data from approximately a dozen patients by the end of 2024. Schwartz also noted that by analyzing data from a larger group of patients, they hope to determine if specific genetic alterations are more sensitive to the drug.