Alethia Young's questions to Adverum Biotechnologies (ADVM) leadership • Q4 2020
Question
Alethia Young of Cantor Fitzgerald inquired about the importance of secondary endpoints, such as the rescue regimen, from both the FDA's and physicians' perspectives, and asked if any interim analyses were planned for the pivotal trials before the 52-week endpoint.
Answer
CMO Aaron Osborne stated there will be no interim analyses for the registrational trials, with the primary endpoint analyzed at one year to support the BLA submission. He emphasized the importance of secondary endpoints, particularly OCT analyses, to demonstrate how the therapy's ability to maintain stability could reduce long-term complications like fibrosis and atrophy, which are linked to fluctuations seen with current treatments.