Colleen Kusy's questions to Karyopharm Therapeutics (KPTI) leadership • Q2 2025
Question
Colleen Kusy from Robert W. Baird & Co. asked for more detail on the higher baseline Total Symptom Score (TSS) in the pivotal myelofibrosis study and its potential impact, and also questioned the rationale behind the observed lower rates of grade 3/4 anemia with the combination therapy.
Answer
Chief Medical Officer Reshma Rangwala explained that historical data suggests a higher baseline TSS is more likely to result in a meaningful clinical outcome, making the current trend in the SENTRY trial encouraging. Regarding anemia, she attributed the lower rates to selinexor's disease-modifying properties, citing prior data showing reductions in key cytokines involved in anemia and preliminary evidence of improved bone marrow health, which could allow for the repopulation of red blood cell precursors.