Jenny Leigh Gonzalez-Armenta's questions to uniQure (QURE) leadership • Q1 2025
Question
Jenny Leigh Gonzalez-Armenta, on for Joseph Schwartz, asked about the new CBER head's views on patient advocacy groups, uniQure's relationship with the Huntington's Disease Society of America, and the general sentiment of the HD community.
Answer
CMO Dr. Walid Abi-Saab emphasized uniQure's long and productive history with patient advocacy groups like CHDI, stating their work and sophisticated natural history data have been essential for the field. He described these organizations as extremely balanced, well-respected by the FDA, and crucial partners, noting that without them, uniQure and others would not be where they are today.