Question · Q3 2025
Justin Smith asked about WAINUA (iplantosin), specifically if the CARDIO-TTRansform trial could reshape long-term treatment guidelines and whether new, simpler diagnostic tests are emerging to expand the cardiomyopathy patient population.
Answer
EVP of Biopharmaceuticals R&D Sharon Barr discussed CARDIO-TTRansform's potential to demonstrate the role of silencers and compare iplantosin with tafamidis, noting ALXN2220 for combination approaches. She also mentioned efforts in earlier diagnosis via AI models and biomarker assays. EVP of Biopharmaceuticals Business Unit Ruud Dobber highlighted it as the largest CM trial, with hopes for a CV mortality benefit.