Mark Connolly's questions to Solid Biosciences (SLDB) leadership • Q3 2020
Question
Mark Connolly of Credit Suisse inquired about the specifics of the manufacturing process improvements, including the previous ratio of full to empty viral capsids, and the company's confidence in scaling up the new process. He also asked for clarity on the IGNITE DMD trial's disclosure timelines, such as the number of patients to be dosed and when data from these new patients might be released.
Answer
CTO Joel Schneider explained that the new manufacturing process now averages 90% full capsids, a significant improvement from the previous ~50%, which reduces the total viral load for patients. He affirmed confidence in scaling the suspension-based method. Acting CMO Cathryn Clary stated that for the next two patients, 30-day data will be reviewed with the DSMB before proceeding with each subsequent patient. CEO Ilan Ganot added that while the company won't provide specific guidance on data release timelines, they are committed to sharing important updates as they become available.