Mick (on behalf of Roanna Ruiz)'s questions to ENANTA PHARMACEUTICALS (ENTA) leadership • Q2 2024
Question
The analyst asked about the enrollment status of the final cohort in the RSVPEDs study and the subsequent data timeline. They also inquired about the desired safety profile and dosing frequency for the future oral KIT inhibitor for CSU.
Answer
The company is in the "home stretch" of enrolling the final cohort (20 patients, aged 28 days to 6 months) for the RSVPEDs study. For the CSU program, they are targeting a once-daily (QD) candidate with a best-in-class safety profile, good potency, and high selectivity, with plans to select the final candidate in Q4.