Omari Baruti's questions to Passage BIO (PASG) leadership • Q4 2022
Question
Omari Baruti from Goldman Sachs asked about the specific outputs from the early infantile high-dose GM1 cohort needed to advance to registrational studies and whether there is any visibility on the potential registrational endpoint.
Answer
CEO Will Chou stated that the key outputs they are looking for are durable decreases in GM1 ganglioside levels and improvements in patient development. Chief Medical Officer Mark Forman added that the specific registrational endpoints will be defined following ongoing discussions with health authorities.