Raju Prasad's questions to ROCKET PHARMACEUTICALS (RCKT) leadership • Q2 2021
Question
Raju Prasad asked about the clinical progression plan for the Danon program now that the high dose is discontinued, specifically regarding adult versus pediatric populations, and requested clarification on changes to the immunosuppression regimen.
Answer
CEO Gaurav Shah stated the company intends to move forward immediately with the pediatric population at the low dose. Regarding the immunosuppression regimen, he described the changes as refinements and tightening of the protocol but declined to provide specifics during an active dialogue with the FDA.