Samantha Corwin's questions to uniQure (QURE) leadership • Q1 2025
Question
Samantha Corwin asked about the long-term strategy for evaluating AMT-130 in earlier or later-stage Huntington's disease and inquired about the number of U.S. physicians capable of performing the administration procedure.
Answer
CMO Dr. Walid Abi-Saab explained that while there is great interest in exploring earlier or later-stage intervention, it's early days and requires discussion with regulators. For administration, he stated that upwards of 50 U.S. sites are capable of performing the MRI-guided intraparenchymal infusion, describing it as a relatively common procedure for neurosurgeons.