Suzanne van Voorthuizen's questions to uniQure (QURE) leadership • Q1 2025
Question
Suzanne van Voorthuizen asked for details on preliminary commercial plans for AMT-130 in the U.S. and inquired about the company's current thinking on a potential European filing or ex-U.S. partnership.
Answer
CEO Matthew Kapusta expressed excitement about the commercial potential for AMT-130 as a first-in-class, disease-modifying therapy. He confirmed the current focus is on U.S. regulatory interactions but they will engage with European regulators. He acknowledged significant strategic interest from large pharma and biotech, stating uniQure will always act in the best interest of shareholders.