Whitney Ijem's questions to PALVELLA THERAPEUTICS (PVLA) leadership • Q2 2025
Question
Whitney Ijem of Canaccord Genuity Inc. asked about the dosing differences for cutaneous venous malformations (CVM) versus microcystic lymphatic malformations (MLM), the relative lesion sizes, and the key criteria used to select new pipeline indications, particularly regarding patient population size.
Answer
Chief Scientific Officer Jeff Martini explained that the dosing is standardized, with one pump actuation covering about 200 cm², up to a maximum of 400 cm² for both indications. President and CEO Wes Kaupinen outlined the selection criteria for new indications, which include a high unmet need (no FDA-approved therapies), a serious impact on quality of life, and an orphan, but not ultra-orphan, patient population.