Question · Q3 2025
Anyan Rama inquired about the expected enrollment curve for the Aurora supportive study for GTX-102 in Angelman syndrome, asking how it might compare to the enrollment observed in the pivotal ASPIRE trial.
Answer
Howard Horn, Chief Financial Officer, anticipated that the Aurora trial would enroll quickly due to high patient interest for its open-label design, contrasting with the sham-controlled ASPIRE study. He noted its importance for gathering data across a wider array of genotypes.
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